4.4(top 10%)
impact factor
1.2K(top 20%)
papers
24.0K(top 10%)
citations
61(top 10%)
h-index
4.5(top 10%)
impact factor
1.5K
all documents
27.4K
doc citations
92(top 10%)
g-index

Top Articles

#TitleJournalYearCitations
1Emerging Issues in AAV-Mediated In Vivo Gene TherapyMolecular Therapy - Methods and Clinical Development2018578
2Global Manufacturing of CAR T Cell TherapyMolecular Therapy - Methods and Clinical Development2017480
3Engineering and Design of Chimeric Antigen ReceptorsMolecular Therapy - Methods and Clinical Development2019281
4Airways Expression of SARS-CoV-2 Receptor, ACE2, and TMPRSS2 Is Lower in Children Than Adults and Increases with Smoking and COPDMolecular Therapy - Methods and Clinical Development2020231
5Production and clinical development of nanoparticles for gene deliveryMolecular Therapy - Methods and Clinical Development2016207
6Manufacturing of recombinant adeno-associated viral vectors for clinical trialsMolecular Therapy - Methods and Clinical Development2016198
7Production of lentiviral vectorsMolecular Therapy - Methods and Clinical Development2016192
8Clinical development of gene therapy: results and lessons from recent successesMolecular Therapy - Methods and Clinical Development2016183
9Prevalence of Pre-existing Antibodies to CRISPR-Associated Nuclease Cas9 in the USA PopulationMolecular Therapy - Methods and Clinical Development2018181
10Capsid Modifications for Targeting and Improving the Efficacy of AAV VectorsMolecular Therapy - Methods and Clinical Development2019168
11Oncolytic Viruses and the Immune System: The Dynamic DuoMolecular Therapy - Methods and Clinical Development2020152
12Improved Loading of Plasma-Derived Extracellular Vesicles to Encapsulate Antitumor miRNAsMolecular Therapy - Methods and Clinical Development2019151
13Long-Term Engraftment and Fetal Globin Induction upon BCL11A Gene Editing in Bone-Marrow-Derived CD34 + Hematopoietic Stem and Progenitor CellsMolecular Therapy - Methods and Clinical Development2017131
14Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector TransductionMolecular Therapy - Methods and Clinical Development2018125
15Pharmacology of Recombinant Adeno-associated Virus ProductionMolecular Therapy - Methods and Clinical Development2018124
16Biocompatible, Purified VEGF-A mRNA Improves Cardiac Function after Intracardiac Injection 1 Week Post-myocardial Infarction in SwineMolecular Therapy - Methods and Clinical Development2018116
17Barriers and Strategies of Cationic Liposomes for Cancer Gene TherapyMolecular Therapy - Methods and Clinical Development2020115
18The Two Faces of ACE2: The Role of ACE2 Receptor and Its Polymorphisms in Hypertension and COVID-19Molecular Therapy - Methods and Clinical Development2020114
19Mesenchymal Stem Cells Overexpressing Interleukin-10 Promote Neuroprotection in Experimental Acute Ischemic StrokeMolecular Therapy - Methods and Clinical Development2017110
20Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human PrimateMolecular Therapy - Methods and Clinical Development2019110
21Integrase-Deficient Lentiviral Vector as an All-in-One Platform for Highly Efficient CRISPR/Cas9-Mediated Gene EditingMolecular Therapy - Methods and Clinical Development2017106
22EU Regulatory Pathways for ATMPs: Standard, Accelerated and Adaptive Pathways to Marketing AuthorisationMolecular Therapy - Methods and Clinical Development2019106
23B-cell depletion is protective against anti-AAV capsid immune response: a human subject case studyMolecular Therapy - Methods and Clinical Development2014101
24Prevalence of Anti-Adeno-Associated Virus Immune Responses in International Cohorts of Healthy DonorsMolecular Therapy - Methods and Clinical Development2019100
25Engineering Nanoparticles for Targeted Delivery of Nucleic Acid Therapeutics in TumorMolecular Therapy - Methods and Clinical Development2019100
26A Rapamycin-Based GMP-Compatible Process for the Isolation and Expansion of Regulatory T Cells for Clinical TrialsMolecular Therapy - Methods and Clinical Development201896
27Thermal Stability as a Determinant of AAV Serotype IdentityMolecular Therapy - Methods and Clinical Development201795
28An Introduction to the Analysis of Single-Cell RNA-Sequencing DataMolecular Therapy - Methods and Clinical Development201895
29A Self-Deleting AAV-CRISPR System for In Vivo Genome EditingMolecular Therapy - Methods and Clinical Development201993
30Empty virions in AAV8 vector preparations reduce transduction efficiency and may cause total viral particle dose-limiting side effectsMolecular Therapy - Methods and Clinical Development201492
31Preclinical development and qualification of ZFN-mediated CCR5 disruption in human hematopoietic stem/progenitor cellsMolecular Therapy - Methods and Clinical Development201691
32Microglia-specific targeting by novel capsid-modified AAV6 vectorsMolecular Therapy - Methods and Clinical Development201691
33Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABsMolecular Therapy - Methods and Clinical Development201989
34Selection of an Efficient AAV Vector for Robust CNS Transgene ExpressionMolecular Therapy - Methods and Clinical Development201989
35Optimizing CAR-T Cell Manufacturing Processes during Pivotal Clinical TrialsMolecular Therapy - Methods and Clinical Development202089
36Universal Method for the Purification of Recombinant AAV Vectors of Differing SerotypesMolecular Therapy - Methods and Clinical Development201888
37Optimizing EphA2-CAR T Cells for the Adoptive Immunotherapy of GliomaMolecular Therapy - Methods and Clinical Development201887
38Development of Intrathecal AAV9 Gene Therapy for Giant Axonal NeuropathyMolecular Therapy - Methods and Clinical Development201885
39Analytical methods for process and product characterization of recombinant adeno-associated virus-based gene therapiesMolecular Therapy - Methods and Clinical Development202185
40Widespread gene transfer in the central nervous system of cynomolgus macaques following delivery of AAV9 into the cisterna magnaMolecular Therapy - Methods and Clinical Development201484
41Adeno-associated viral vectors do not efficiently target muscle satellite cellsMolecular Therapy - Methods and Clinical Development201484
42Moving oncolytic viruses into the clinic: clinical-grade production, purification, and characterization of diverse oncolytic virusesMolecular Therapy - Methods and Clinical Development201683
43Disruption of the BCL11A Erythroid Enhancer Reactivates Fetal Hemoglobin in Erythroid Cells of Patients with β-Thalassemia MajorMolecular Therapy - Methods and Clinical Development201883
44INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular GenomesMolecular Therapy - Methods and Clinical Development201781
45Methods Matter: Standard Production Platforms for Recombinant AAV Produce Chemically and Functionally Distinct VectorsMolecular Therapy - Methods and Clinical Development202080
46Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus MacaquesMolecular Therapy - Methods and Clinical Development201879
47A Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular DystrophyMolecular Therapy - Methods and Clinical Development201778
48The Pharmacology of T Cell TherapiesMolecular Therapy - Methods and Clinical Development201878
49Expression of Human ACE2 in Lactobacillus and Beneficial Effects in Diabetic Retinopathy in MiceMolecular Therapy - Methods and Clinical Development201978
50Development of a Novel Anti-CD19 Chimeric Antigen Receptor: A Paradigm for an Affordable CAR T Cell Production at Academic InstitutionsMolecular Therapy - Methods and Clinical Development201977